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GCL is made of two subunits (GCLC (a catalytic subunit) and GCLM (a modifier subunit))

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Cell Rep (2022) 40(3):111128

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Williams is serving as sponsor investigator for a number of human gene therapy trials at CHB, including in SCID-X1, Wiskott-Aldrich Disease, Childhood Cerebral Adrenoleukodystropy and a trial in sickle cell disease targeting the transcription factor BCL11a

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3 (120 mg, 0.47 mmol, 1.3 eq.) was added and stirred at 40 C under Ar for 24 h

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