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Phan TT, Abozguia K, Shivu GN, Mahadevan G, Ahmed I, Williams L, et al

Louis, MO) via subcutaneous (s.c.) injection 5 days a week for 4 weeks as detailed in Supplementary Table 2

[Medium-chain acyl-CoA-dehydrogenase (MCAD) deficiency: French consensus for neonatal screening, diagnosis, and management]

The appeal of AAS in this population is largely attributable to the promise of rapid and pronounced increases in muscle mass
